Amicus Therapeutics is pioneering a paradigm-shifting approach to treating a range of human genetic diseases in which crucial proteins are misfolded, thus reducing or eliminating their functionality. Amicus develops pharmacological chaperones - oral therapies that bind to and stabilize the affected proteins, restoring their shape, proper trafficking, and biological activity. This novel, next-generation approach offers the potential to improve treatment options for patients with genetic diseases.

IISC is a non-profit organisation that
partners with individuals, organizations
and communities to achieve greater
social impact. It does this through providing training, facilitation and coaching services to the public and not-for-profit sectors.

Sanders & Clients BV
is a Dutch company that deliver equipment to infuse the medicine.